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1 research outputs found
Targeted mRNA Therapy for Ornithine Transcarbamylase Deficiency
Author
Adami
Allen G. Li
+66聽more
Amber E. Paschal
Anna Galperin
Asano
Ashwell
Baba
Calcedo
Cheng
Chiefari
Convertine
Convertine
Cunningham
Cunningham
Cunningham
Debashish Roy
DeRosa
El-Gharbawy
Eric C. Bell
Fenton
Garc铆a-P茅rez
Gernoux
Hacein-Bey-Abina
Hardee
Hodges
Houseley
Immordino
Jean-Rene Ella-Menye
Jurk
Karik贸
Karik贸
Kauffman
Lichter-Konecki
Lundy
Manno
Martins
Mary G. Prieve
Matt Waldheim
Michael E. Houston
Mingozzi
Mishra
Nathwani
Pardi
Pardi
Pierrot Harvie
Ramaswamy
Raper
Rosenberg
Rozema
Rozema
Sahin
Schwartz
Sean D. Monahan
Seymour
Su
Teri L. Blevins
Thran
Uchida
Vallazza
Vandamme
Vannucci
Wang
Weissman
Whitehead
Wong
Yang
Ye
Youssef
Publication venue
'Elsevier BV'
Publication date
Field of study
No full text
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