1 research outputs found
Transatlantic combined and comparative data analysis of 1095 patients with urea cycle disorders : a successful strategy for clinical research of rare diseases
- Author
- Alber Fabienne Dietrich
- Arnoux Jean-Baptiste
- Babikian Talin
- Baric Ivo
- Batshaw Mark L.
- Baumgartner Matthias R.
- Bender Heidi
- Berry Susan A.
- Bloxam Sondra
- Bosch Annet M.
- Boy Nikolas
- Boys Christopher
- Breiger David
- Brody Linnea
- Buerger Corinna
- Burgard Peter
- Burlina Alberto B.
- Burrage Lindsay
- Caspi Liora
- Caudle Susan E.
- Cederbaum Stephen
- Chabrol Brigitte
- Chakrapani Anupam
- Cortes-Saladefont Elisenda
- Couce Maria L.
- Coughlin Curtis
- de Laet Corine
- de Lonlay Pascale
- de Meirleir Linda
- Diaz George A.
- Dionisi-Vici Carlo
- Dobbelaere Dries
- Elsbecker Sara
- Eyskens Fran\ue7ois
- Feigenbaum Annette
- Fierro Luca
- Freisinger Peter
- Gallagher Renata C.
- Garbade Sven F.
- Garcia-Cazorla Angeles
- Gleich Florian
- Gropman Andrea
- Grunewald Stephanie
- Haberle Johannes
- Harding Cary O.
- Hoffmann Georg F.
- Hwu Wuh-Liang
- Jalan Anil
- Karall Daniela
- Kerr Douglas S.
- Kerr Elizabeth
- Koelker Stefan
- Le Mons Cynthia
- Lee Brendan
- Lichter-Konecki Uta
- Lindner Martin
- Lund Allan M.
- Lynn Audrey
- Mamak Eva
- Martinelli Diego
- McCandless Shawn
- Merritt J. Lawrence, II
- Mew Nicholas Ah.
- Muehlhausen Chris
- Mullins Mary
- Murphy Elaine
- Mutze Ulrike
- Nagamani Sandesh C. S.
- Nguyen-Driver Mina
- Olivieri Giorgia
- Ottolenghi Chris
- Papaleo Cassandra
- Payan Irma
- Posset Roland
- Rodrigues Esmeralda
- Rubert Laura
- Sanz Jacqueline H.
- Sarajlija Adrijan
- Schiff Manuel
- Schulze Andreas
- Seashore Margretta R.
- Seminara Jennifer
- Simpson Kara
- Singer Rebecca
- Sokal Etienne
- Stricker Tamar
- Summar Marshall
- Sykut-Cegielska Jolanta
- Tangen Rachel
- Teles Elisa Leao
- Tuchman Mendel
- Vara Roshni
- Waisbren Susan
- Wallis Kimberly
- Walter John H.
- Weisfeld-Adams James
- Wilkening Greta
- Williams Monique
- Wong Derek
- Yudkoff Marc
- Zeman Jiri
- Publication venue
- Publication date
- 01/01/2019
- Field of study