Transatlantic combined and comparative data analysis of 1095 patients with urea cycle disorders : a successful strategy for clinical research of rare diseases
- Authors
- Fabienne Dietrich Alber
- Jean-Baptiste Arnoux
- Talin Babikian
- Ivo Baric
- Mark L. Batshaw
- Matthias R. Baumgartner
- Heidi Bender
- Susan A. Berry
- Sondra Bloxam
- Annet M. Bosch
- Nikolas Boy
- Christopher Boys
- David Breiger
- Linnea Brody
- Corinna Buerger
- Peter Burgard
- Alberto B. Burlina
- Lindsay Burrage
- Liora Caspi
- Susan E. Caudle
- Stephen Cederbaum
- Brigitte Chabrol
- Anupam Chakrapani
- Elisenda Cortes-Saladefont
- Maria L. Couce
- Curtis Coughlin
- Corine de Laet
- Pascale de Lonlay
- Linda de Meirleir
- George A. Diaz
- Carlo Dionisi-Vici
- Dries Dobbelaere
- Sara Elsbecker
- Fran\ue7ois Eyskens
- Annette Feigenbaum
- Luca Fierro
- Peter Freisinger
- Renata C. Gallagher
- Sven F. Garbade
- Angeles Garcia-Cazorla
- Florian Gleich
- Andrea Gropman
- Stephanie Grunewald
- Johannes Haberle
- Cary O. Harding
- Georg F. Hoffmann
- Wuh-Liang Hwu
- Anil Jalan
- Daniela Karall
- Douglas S. Kerr
- Elizabeth Kerr
- Stefan Koelker
- Cynthia Le Mons
- Brendan Lee
- Uta Lichter-Konecki
- Martin Lindner
- Allan M. Lund
- Audrey Lynn
- Eva Mamak
- Diego Martinelli
- Shawn McCandless
- J. Lawrence, II Merritt
- Nicholas Ah. Mew
- Chris Muehlhausen
- Mary Mullins
- Elaine Murphy
- Ulrike Mutze
- Sandesh C. S. Nagamani
- Mina Nguyen-Driver
- Giorgia Olivieri
- Chris Ottolenghi
- Cassandra Papaleo
- Irma Payan
- Roland Posset
- Esmeralda Rodrigues
- Laura Rubert
- Jacqueline H. Sanz
- Adrijan Sarajlija
- Manuel Schiff
- Andreas Schulze
- Margretta R. Seashore
- Jennifer Seminara
- Kara Simpson
- Rebecca Singer
- Etienne Sokal
- Tamar Stricker
- Marshall Summar
- Jolanta Sykut-Cegielska
- Rachel Tangen
- Elisa Leao Teles
- Mendel Tuchman
- Roshni Vara
- Susan Waisbren
- Kimberly Wallis
- John H. Walter
- James Weisfeld-Adams
- Greta Wilkening
- Monique Williams
- Derek Wong
- Marc Yudkoff
- Jiri Zeman
- Publication date
- 1 January 2019
- Publisher