1 research outputs found
Safety and efficacy of avalglucosidase alfa versus alglucosidase alfa in patients with late-onset Pompe disease (COMET): a phase 3, randomised, multicentre trial
- Author
- Alonso-Perez J
- Altemus P
- Attarian S
- Aube-Nathier A-C
- Avelar JB
- Bailey C
- Behin A
- Bekircan-Kurt CE
- Berger KI
- Billy J
- Boentert M
- Borges JL
- Boschi S
- Bouhour F
- Brown KE
- Carrera Garcia L
- Carvalho G
- Chahin N
- Charrow J
- Chase L
- Chien Y-H
- Choi YC
- Cirne H
- Clemens PR
- Danjoux L
- Davion J-B
- Day JW
- DeArmey S
- Deegan P
- Diaz-Manera J
- Dimachkie MM
- Durmus Tekce H
- Duval F
- Erdem-Ozdamar S
- Fedotova E
- Gandolfo E
- Genge A
- Goker-Alpan O
- Grosz Z
- Guellec D
- Guettsches A-K
- Guglieri M
- Gutmann L
- Haack KA
- Hatcher E
- Helms S
- Henderson RD
- Hennermann JB
- Hiwot T
- Hufgard-Leitner M
- Hug C
- Hughes D
- Huynh-Ba O
- Illarioshkin S
- Johnson J
- Karaa A
- Karam C
- Kautzky-Willer A
- Kishnani PS
- Klyushnikov SA
- Komaki H
- Kostera-Pruszczyk A
- Kushlaf H
- Ladha S
- Laforet P
- Langton J
- Linkova L
- Longo N
- Malinova V
- Mare R
- Mavroudakis N
- Maxit C
- Mazurova S
- Mengel E
- Moggio MG
- Molnar MJ
- Mongini TE
- Mori M
- Mozaffar T
- Muller-Miny L
- Musumeci O
- Nadaj-Pakleza A
- Nance CS
- Nascimento Osorio A
- Natera-de Benito D
- Neel R
- Niizawa GA
- Noll L
- Noury J-B
- Oliveira ASB
- Ortega E
- Parman Y
- Pasnoor M
- Pautot V
- Pena L
- Potulska-Chromik A
- Pugliese A
- Questienne C
- Ramos Lopes M
- Remiche G
- Reyes-Leiva D
- Riedl M
- Roberts M
- Rugiero MF
- Salort-Campana E
- Schoser B
- Sciacco M
- Sgobbi Souza PV
- Shieh PB
- Smith C
- Sole G
- Solera L
- Souto Lopes S
- Specht S
- Statland J
- Straub V
- Stulnig T
- Swenson A
- Taithe F
- Tan CY
- Tard C
- Tarnopolsky M
- Thibault N
- Tizon S
- Toscano A
- van der Beek NAME
- van der Ploeg AT
- van Kooten HA
- Vorgerd M
- Wencel M
- Wenninger S
- Whitley C
- Young P
- Zagnoli F
- Zhou T
- Publication venue
- Elsevier Ltd
- Publication date
- Field of study