64 research outputs found
Faculty Opinions recommendation of A self-inactivating lentiviral vector for SCID-X1 gene therapy that does not activate LMO2 expression in human T cells.
No full textFaculty Opinions recommendation of Increasing the efficiency of homology-directed repair for CRISPR-Cas9-induced precise gene editing in mammalian cells.
No full textFaculty Opinions recommendation of Enhanced homology-directed human genome engineering by controlled timing of CRISPR/Cas9 delivery.
No full textFaculty Opinions recommendation of A high-throughput chemical screen with FDA approved drugs reveals that the antihypertensive drug Spironolactone impairs cancer cell survival by inhibiting homology directed repair.
No full textFaculty Opinions recommendation of mRNA-mediated gene delivery into human progenitor cells promotes highly efficient protein expression.
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Faculty Opinions recommendation of The use of chromatin insulators to improve the expression and safety of integrating gene transfer vectors.
No full textFaculty Opinions recommendation of Novel fluorescent genome editing reporters for monitoring DNA repair pathway utilization at endonuclease-induced breaks.
No full textFaculty Opinions recommendation of Production of Gene-Corrected Adult Beta Globin Protein in Human Erythrocytes Differentiated from Patient iPSCs After Genome Editing of the Sickle Point Mutation.
No full textFaculty Opinions recommendation of Tracking genome engineering outcome at individual DNA breakpoints.
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