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1 research outputs found
Safety, tolerability, and efficacy of a widely available nusinersen program for Polish children with spinal muscular atrophy
Author
Biedroń Agnieszka
Boćkowski Leszek
+18 more
Chmielewski Dariusz
Cichosz Dorota
Czyżyk Elżbieta
Dudzińska Magdalena
Gadowska Elżbieta
Jasiński Mirosław
Kempisty Agnieszka
Kostera-Pruszczyk Anna
Kotulska Katarzyna
Masztalerz Anna
Mazurkiewicz-Bełdzińska Maria
Młynarczyk Elżbieta
Pierzchlewicz Katarzyna
Pietruszewski Jerzy
Przysło Łukasz
Rabczenko Daniel
Steinborn Barbara
Tomaszek Katarzyna
Publication venue
'Elsevier BV'
Publication date
01/01/2022
Field of study
No full text
Jagiellonian Univeristy Repository