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1 research outputs found
Mapping the differences in care for 5,000 Spinal Muscular Atrophy patients, a survey of 24 national registries in North America, Australasia and Europe
Author
Alejandro M
Ambrosini A
+60Â more
Angelkova N
Beroud C
Bladen CL
Bloetzer C
Bushby K
Butoianu N
Campbell C
Chamova T
Chertkoff L
Craiu D
Cuisset JM
Dawkins H
Enriquez GVG
Garami M
Garland C
Gredal O
Guergueltcheva V
Haberlova J
Herczegfalvi A
Jackson JM
Jeannet PY
Jedrzejowska M
Jimenez A
Karaduman A
Karcagi V
Kirschner J
Klein A
Korngut L
Kosac A
Kostera-Pruszczyk A
Lahdetie J
Lochmuller H
Lusakowska A
Matyushenko V
Mercuri E
Monges S
Moresco A
Nascimento A
Ortiz GG
Pisano P
Rafferty K
Rasic VM
Rodrigues M
Roxburgh R
Salgado D
Saugier-Veber P
Schreiber O
Sejersen T
Straub V
Strenkova J
Thompson R
Tizzano E
Topaloglu H
van der Pol L
Verschuuren J
Wadman RI
Walter MC
Wegel C
Yilmaz O
Youngs L
Publication venue
'Springer Fachmedien Wiesbaden GmbH'
Publication date
Field of study
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