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Effect of cyclic, low dose pyrimethamine treatment in patients with Late Onset Tay Sachs: an open label, extended pilot study

Authors
  1. A Bøyum
  2. Ari Zimran
  3. Avi Valevski
  4. Aviva Fattal-Valevski
  5. BE Shapiro
  6. BR Brooks
  7. C1 Leport
  8. Deborah Elstein
  9. E Osher
  10. Etty Osher
  11. GH1 Maegawa
  12. HW Kresse
  13. ILO Buxton
  14. JT Clarke
  15. Leah Peleg
  16. Liora Sagie
  17. LM Weiss
  18. LM Weiss
  19. M Tinetti
  20. MB Tropak
  21. ME Tinetti
  22. Nadav Sagiv
  23. Naftali Stern
  24. Nataly Urshanski
  25. O1 Neudorfer
  26. P1 Leinekugel
  27. R Gravel
  28. Ruth Navon
  29. SL Hauser
  30. Tally Lerman-Sagie
Publication date
Publisher
'Springer Science and Business Media LLC'
Doi

    Abstract

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      oaiinfo:doi/10.1186%2Fs13023-015-...
      Last time updated on 05/06/2019

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