The Therapeutic Implications of Muscular Dystrophy Genomics

Abstract

With an introduction by Professor Jan Witkowski, this Witness Seminar transcript presents an account of the therapeutic implications of muscular dystrophy genomics. The participants provide insights into the clinical and genetic characterizations of muscular dystrophy, with a particular emphasis on Duchenne muscular dystrophy, and shed light on the research coordination and the recent approaches towards the treatment of this group of devastating pathological entities