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13 research outputs found
Pharmacogenomic Biomarkers: an FDA Perspective on Utilization in Biological Product Labeling
Author
A Agarwal
C Grimstein
+16 more
CM Walko
E Louis
FJ Sasinowski
GS Pandey
I Zineh
I Zineh
JD Mellor
Joseph A. Grillo
MA Pacanowski
MA Pacanowski
P Carter
PD Maher
RJ Keizer
Robert N. Schuck
S Shi
VL Simhadri
Publication venue
'American Association of Pharmaceutical Scientists (AAPS)'
Publication date
Field of study
No full text
Crossref
Genome-wide DNA methylation profiling shows a distinct epigenetic signature associated with lung macrophages in cystic fibrosis
Author
AA Tarique
AD Barrow
+43 more
BT Kopp
C Auffray
C Logie
C Wu
C Xia
CJ Marsit
D Aldinucci
E Merck
E Osika
EA Houseman
EA Houseman
EM Bruscia
HH Oz
HJ Kim
J Wang
JA Dewhurst
JL Bessich
K Simonin-Le Jeune
KD Pfeffer
L Paemka
LA Pennacchio
LP Nicod
M Cabanel
M Gardiner-Garden
M Magalhaes
M Mohrs
M Ost
MJ Aryee
MM Monick
N Rieber
NA Kittan
R Donato
RW Vandivier
RW Vandivier
S Kolahian
S Maxeiner
SA Gharib
SC Zheng
SD Sagel
T Bonfield
T Kling
TL Bonfield
VL Simhadri
Publication venue
'Springer Science and Business Media LLC'
Publication date
Field of study
No full text
Crossref
Multifunctional CRISPR-Cas9 with engineered immunosilenced human T cell epitopes
Author
A Dobin
AT Martino
+51 more
C King
C Trapnell
CD Scallan
CS Manno
D Chowell
D Cyranoski
D Wang
Dimitrios L. Wagner
E Marshall
F Mingozzi
F Mingozzi
F Mingozzi
G Gao
H Jiang
H Mok
H Nishimasu
H Yin
HB Gaspar
HG Rammensee
HK Liao
I Hoof
J Levitskaya
J Wang
JR Cantor
JR Carapetis
JW Yewdell
KS Anderson
LE Mays
M Bartel
M Cavazzana-Calvo
M Moutaftsi
M Wolfl
MA Kay
MD Robinson
R Mazor
R Thwaite
R Vita
RS Salvat
S Boutin
S Hacein-Bey-Abina
S Tangri
S Tenzer
SH Ibrahim
SJ Howe
VL Simhadri
VP Yeung
W Humphrey
Wei Leong Chew
WL Chew
Y Zheng
YS Ahi
Publication venue
'Springer Science and Business Media LLC'
Publication date
Field of study
No full text
Crossref
Extracellular nanovesicles for packaging of CRISPR-Cas9 protein and sgRNA to induce therapeutic exon skipping
Author
A Tanaka
AI Nesvizhskii
+51 more
AR Ferré-D’Amaré
C Long
C Montagna
C Voelkel
CA Schneider
CE Nelson
CE Nelson
D-T Wu
DS Ory
DW Huang
G Buchlis
G Petris
GJ Knott
H Hahne
H Ma
H Xu
HL Li
HL Li
J Fuenmayor
J Rappsilber
JAG Briggs
JG Choi
JH Bayle
K Imamura
K Ishida
K Rapti
L Amoasii
L Pinello
L Villiger
LA Campbell
M Iwasaki
M Jinek
M Kuzembayeva
M Putyrski
M Tabebordbar
PD Hsu
PE Mangeot
S Guiraud
S Kim
S Yoshioka
SR Witting
T Aoki
T Uchimura
TJ Cradick
V Louis Jeune
VL Simhadri
W Klingler
Y Cai
Y Cai
Y Fu
Z Wu
Publication venue
'Springer Science and Business Media LLC'
Publication date
Field of study
No full text
Crossref
High prevalence of Streptococcus pyogenes Cas9-reactive T cells within the adult human population
Author
A Moosmann
A Schoenbrunn
+49 more
AC Komor
AM Sherwood
B Hammoud
BP Kleinstiver
CA Vakulskas
CL Bennett
DBT Cox
Desiree J. Wendering
Dimitrios L. Wagner
DR Johnson
ES Sen
FA Ran
H Lei
Hans-Dieter Volk
HE Heslop
HS Robins
JK Polansky
JR Carapetis
K Wing
L Guilherme
Leila Amini
Levent Akyüz
Lisa-Marie Burkhardt
M Frentsch
M Jinek
M Johnson
M Schmueck-Henneresse
M Wolfl
Michael Schmueck-Henneresse
MY Yousfi Monod
N Shaikh
OJ Harrison
P Bacher
P Bacher
P Mali
Petra Reinke
R Hamano
S Chandran
S Hori
S Lehrman
S Nayak
S Sakaguchi
S Shmakov
SJ Wakelin
SK Lathrop
VL Simhadri
VR Arruda
WL Chew
WL Chew
Publication venue
'Springer Science and Business Media LLC'
Publication date
Field of study
No full text
Crossref
Considerations in the Use of Codon Optimization for Recombinant Protein Expression
Author
A Dana
A Dana
+62 more
A Hoekema
A Rodriguez
A Villalobos
AA Bazzini
AE Firth
AJ Diaz de Arce
AL Yablonovitch
B Wang
BM Schmitt
BV Ayyar
C Kimchi-Sarfaty
C Li
C Ling
C McCarthy
CE Gamble
CH Yu
D Matsuda
D Paulet
DE Cheong
E Alkalaeva
E Angov
E Goldman
E Jan
E Wang
E Zucchelli
ED Kelsic
F Pouyet
F Supek
FK Lorenz
H Gingold
H Wang
J Fang
JA Williams
K Kelen Van Der
KL Rudolph
KM Chacón
L Fabritus de
L Kotula
M Ensterö
M Gehrmann
M Stadler
M Welch
M Zhou
MA Martínez
NT Ingolia
R Fahraeus
RA Cripwell
S Apcher
S Kirchner
S Malarkannan
SA Chappell
SA Chappell
SM Richardson
SR Starck
V Bali
V Presnyak
VL Simhadri
VP Mauro
Y Harigaya
Y Hashem
Z Zhou
ZR Newman
Publication venue
'Springer Science and Business Media LLC'
Publication date
Field of study
No full text
Crossref
Personalized Prevention Strategies to Defeat Cancer
Author
A Canossi
A Miranda-Vizuete
+75 more
A Patenaude
AM Berghella
AM Berghella
AM Berghella
AM Berghella
AM Berghella
C Biguet
CL Bennett
CT Weaver
D Bray
D Mustacich
DL Cheng
E Volpe
EC Nowak
G Powis
G Powis
GA Peltz
H Masutani
H Muta
H Schenk
HR Koene
I Contasta
I Contasta
J Li
JG van de Winkel
JM Greer
JR Matthews
JV Ravetch
K Hirota
KA Janes
KA Janes
KM Murphy
L Yang
L Zhou
LA Schubert
M Alzona
M Benhar
M Carrington
M Saitoh
M Veldhoen
ML Ericson
MT Wong
N Gleicher
N Manel
N Wakasugi
P Parham
P Pellegrini
P Pellegrini
P Pellegrini
P Pellegrini
PG Hargreaves
PH Salim
PP McDonald
PW Parren
R Bertini
R Biassoni
R Singh
S Gromer
S Kulkarni
S Kusmartsev
S Mostafa
S Toloza
SB Kanaan
T Del Beato
T Hayashi
T Korn
T Korn
U Schwertassek
V Dardalhon
VL Simhadri
W Ekström
WQ Qiu
X Zhou
Y Zhou
YM Deo
Publication venue
'Springer Science and Business Media LLC'
Publication date
Field of study
No full text
Crossref
Diversifying the structure of zinc finger nucleases for high-precision genome editing
Author
A Gupta
AC Jamieson
+74 more
AI Hollander den
AJ Wood
B Diez
B Zetsche
BP Kleinstiver
CM Johnson
D Hockemeyer
DA Wah
DE Bauer
DJ Segal
DJ Segal
DL DiGiusto
E Kim
EE Perez
EJ Rebar
F Jacob
F Soldner
FD Urnov
GX Ruan
H Hirano
H Li
H Torikai
H Torikai
HJ Kim
J Guo
J Vierstra
JB Doyon
JC Miller
JD Beane
JD Sander
JD Sander
JG Gilman
JS Kim
JY Dong
K Laoharawee
K Yusa
KH Chang
L Yang
M Bibikova
M Bibikova
M Bibikova
M Elrod-Erickson
M Overbeek van
MD Ryan
MD Simon
MH Porteus
ML Maeder
MT Nilsson
NP Pavletich
P Perez-Pinera
R Sharma
RM Yarrington
RR Beerli
S Mastaglio
S Tabor
S Tan
SM O’Donnell
SQ Tsai
SS Ravin De
TJ Laskowski
V Pattanayak
VK Shukla
VL Simhadri
W Nomura
WJ Etten Van
X Liang
Y Choo
Y Choo
Y Doyon
Y Doyon
Y Doyon
Y Nakagawa
YG Kim
Z Chen
Publication venue
'Springer Science and Business Media LLC'
Publication date
Field of study
No full text
Crossref
CRISPR/Cas9 for Sickle Cell Disease: Applications, Future Possibilities, and Challenges
Author
A Fujita
A Hendel
+97 more
A M Scharenberg
A Paikari
AF Ferreira
B Roy
B Wiedenheft
B Zetsche
BG Forget
BL Stoddard
BP Kleinstiver
BP Kleinstiver
BP Kleinstiver
C Anders
C Antoniani
C Jiang
C Li
C Li
C Saenz
CA Vakulskas
CR Cromwell
DE Bauer
DP Dever
E Gluckman
EB Esrick
EB Esrick
EC Smith
F Adikusuma
FA Ran
FA Ran
FB Piel
FD Urnov
G Shim
G Stamatoyannopoulos
GE Martyn
H Nishimasu
H Yin
HY Shin
I Fonfara
I Tasan
IM Slaymaker
J Watson
J Wen
JC Tsang
JD Grevet
JH Hu
JK Lee
JS Chen
K Lobner
LA Smith
M Bhatia
M Jinek
M Kosicki
M Rahdar
M Uda
M Walters
MA DeWitt
MC Canver
MC Walters
MD Hoban
MD Hoban
MH Steinberg
MM Hsieh
N Liu
N Psatha
O Humbert
P Chatterjee
P Liu
Q Li
R Sugimura
RE Ware
RO Bak
RT Leenay
S Chakrabarti
S Demirci
S Hirano
S Kim
S Lanzkron
S Menzel
S Park
SA Zimmerman
SD Arnold
SK Ballas
SQ Tsai
SQ Tsai
ST Paulukonis
T Masuda
V Pattanayak
VG Sankaran
VL Simhadri
WC Wang
X Huang
X Lan
X Wang
Y Fu
Y Fu
Y Nihongaki
YB Kim
Z Glass
Publication venue
'Springer Science and Business Media LLC'
Publication date
Field of study
No full text
Crossref
Design of efficacious somatic cell genome editing strategies for recessive and polygenic diseases
Author
A Herzog
A Kulesa
+93 more
A Li
AE Carpenter
AL Firth
AV Anzalone
B Lee
B Steyer
B Wang
BP Kleinstiver
BP Kleinstiver
C Albayrak
C Seeger
C Yu
C-Q Song
CD Richardson
CD Sago
CE Nelson
CR Warren
CT Charlesworth
D Yang
DBT Cox
DG Ousterout
DL Wagner
E Liu
E Martin-Touaux
E van der Wal
E van der Wal
F Allen
F Ran
F Xu
FA Ran
H Azuma
H Li
H Yin
H Yin
H Zhu
HW Yang
IM Slaymaker
IY Chen
J Carlson-Stevermer
J Carlson-Stevermer
J Hemphill
J Park
J Sha
J-A Lim
J-A Ribeil
JE Bond
JG Doench
JH Shin
JW Youm
K Saha
KK Raval
KM Davis
L Villiger
LB Harrington
M Cui
M Kosicki
MK Cromer
ML Maeder
MP Zafra
MW Popp
MW Shen
N Raben
OA Bodamer
P Kishnani
PS Kishnani
PS Kishnani
R Cloney
R Ibraheim
RT Walton
S Han
S Hoops
S Lin
S Matsumoto
S Matsumoto
S Torriano
SQ Tsai
SSD Ravin
T Gutschner
T Harkness
T Wei
TT Duong
V Pattanayak
V Prakash
VL Simhadri
VT Chu
WL Chew
WT Hendriks
X Lian
X Liang
Y Fukuhara
Y Rui
Y Yang
YK Katare
Publication venue
'Springer Science and Business Media LLC'
Publication date
Field of study
No full text
Crossref
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