9 research outputs found
Pharmacogenomic Biomarkers: an FDA Perspective on Utilization in Biological Product Labeling
- Author
- Publication venue
- 'American Association of Pharmaceutical Scientists (AAPS)'
- Publication date
- Field of study
Genome-wide DNA methylation profiling shows a distinct epigenetic signature associated with lung macrophages in cystic fibrosis
- Author
- AA Tarique
- AD Barrow
- BT Kopp
- C Auffray
- C Logie
- C Wu
- C Xia
- CJ Marsit
- D Aldinucci
- E Merck
- E Osika
- EA Houseman
- EA Houseman
- EM Bruscia
- HH Oz
- HJ Kim
- J Wang
- JA Dewhurst
- JL Bessich
- K Simonin-Le Jeune
- KD Pfeffer
- L Paemka
- LA Pennacchio
- LP Nicod
- M Cabanel
- M Gardiner-Garden
- M Magalhaes
- M Mohrs
- M Ost
- MJ Aryee
- MM Monick
- N Rieber
- NA Kittan
- R Donato
- RW Vandivier
- RW Vandivier
- S Kolahian
- S Maxeiner
- SA Gharib
- SC Zheng
- SD Sagel
- T Bonfield
- T Kling
- TL Bonfield
- VL Simhadri
- Publication venue
- 'Springer Science and Business Media LLC'
- Publication date
- Field of study
Multifunctional CRISPR-Cas9 with engineered immunosilenced human T cell epitopes
- Author
- A Dobin
- AT Martino
- C King
- C Trapnell
- CD Scallan
- CS Manno
- D Chowell
- D Cyranoski
- D Wang
- Dimitrios L. Wagner
- E Marshall
- F Mingozzi
- F Mingozzi
- F Mingozzi
- G Gao
- H Jiang
- H Mok
- H Nishimasu
- H Yin
- HB Gaspar
- HG Rammensee
- HK Liao
- I Hoof
- J Levitskaya
- J Wang
- JR Cantor
- JR Carapetis
- JW Yewdell
- KS Anderson
- LE Mays
- M Bartel
- M Cavazzana-Calvo
- M Moutaftsi
- M Wolfl
- MA Kay
- MD Robinson
- R Mazor
- R Thwaite
- R Vita
- RS Salvat
- S Boutin
- S Hacein-Bey-Abina
- S Tangri
- S Tenzer
- SH Ibrahim
- SJ Howe
- VL Simhadri
- VP Yeung
- W Humphrey
- Wei Leong Chew
- WL Chew
- Y Zheng
- YS Ahi
- Publication venue
- 'Springer Science and Business Media LLC'
- Publication date
- Field of study
Extracellular nanovesicles for packaging of CRISPR-Cas9 protein and sgRNA to induce therapeutic exon skipping
- Author
- A Tanaka
- AI Nesvizhskii
- AR Ferré-D’Amaré
- C Long
- C Montagna
- C Voelkel
- CA Schneider
- CE Nelson
- CE Nelson
- D-T Wu
- DS Ory
- DW Huang
- G Buchlis
- G Petris
- GJ Knott
- H Hahne
- H Ma
- H Xu
- HL Li
- HL Li
- J Fuenmayor
- J Rappsilber
- JAG Briggs
- JG Choi
- JH Bayle
- K Imamura
- K Ishida
- K Rapti
- L Amoasii
- L Pinello
- L Villiger
- LA Campbell
- M Iwasaki
- M Jinek
- M Kuzembayeva
- M Putyrski
- M Tabebordbar
- PD Hsu
- PE Mangeot
- S Guiraud
- S Kim
- S Yoshioka
- SR Witting
- T Aoki
- T Uchimura
- TJ Cradick
- V Louis Jeune
- VL Simhadri
- W Klingler
- Y Cai
- Y Cai
- Y Fu
- Z Wu
- Publication venue
- 'Springer Science and Business Media LLC'
- Publication date
- Field of study
High prevalence of Streptococcus pyogenes Cas9-reactive T cells within the adult human population
- Author
- A Moosmann
- A Schoenbrunn
- AC Komor
- AM Sherwood
- B Hammoud
- BP Kleinstiver
- CA Vakulskas
- CL Bennett
- DBT Cox
- Desiree J. Wendering
- Dimitrios L. Wagner
- DR Johnson
- ES Sen
- FA Ran
- H Lei
- Hans-Dieter Volk
- HE Heslop
- HS Robins
- JK Polansky
- JR Carapetis
- K Wing
- L Guilherme
- Leila Amini
- Levent Akyüz
- Lisa-Marie Burkhardt
- M Frentsch
- M Jinek
- M Johnson
- M Schmueck-Henneresse
- M Wolfl
- Michael Schmueck-Henneresse
- MY Yousfi Monod
- N Shaikh
- OJ Harrison
- P Bacher
- P Bacher
- P Mali
- Petra Reinke
- R Hamano
- S Chandran
- S Hori
- S Lehrman
- S Nayak
- S Sakaguchi
- S Shmakov
- SJ Wakelin
- SK Lathrop
- VL Simhadri
- VR Arruda
- WL Chew
- WL Chew
- Publication venue
- 'Springer Science and Business Media LLC'
- Publication date
- Field of study
Diversifying the structure of zinc finger nucleases for high-precision genome editing
- Author
- A Gupta
- AC Jamieson
- AI Hollander den
- AJ Wood
- B Diez
- B Zetsche
- BP Kleinstiver
- CM Johnson
- D Hockemeyer
- DA Wah
- DE Bauer
- DJ Segal
- DJ Segal
- DL DiGiusto
- E Kim
- EE Perez
- EJ Rebar
- F Jacob
- F Soldner
- FD Urnov
- GX Ruan
- H Hirano
- H Li
- H Torikai
- H Torikai
- HJ Kim
- J Guo
- J Vierstra
- JB Doyon
- JC Miller
- JD Beane
- JD Sander
- JD Sander
- JG Gilman
- JS Kim
- JY Dong
- K Laoharawee
- K Yusa
- KH Chang
- L Yang
- M Bibikova
- M Bibikova
- M Bibikova
- M Elrod-Erickson
- M Overbeek van
- MD Ryan
- MD Simon
- MH Porteus
- ML Maeder
- MT Nilsson
- NP Pavletich
- P Perez-Pinera
- R Sharma
- RM Yarrington
- RR Beerli
- S Mastaglio
- S Tabor
- S Tan
- SM O’Donnell
- SQ Tsai
- SS Ravin De
- TJ Laskowski
- V Pattanayak
- VK Shukla
- VL Simhadri
- W Nomura
- WJ Etten Van
- X Liang
- Y Choo
- Y Choo
- Y Doyon
- Y Doyon
- Y Doyon
- Y Nakagawa
- YG Kim
- Z Chen
- Publication venue
- 'Springer Science and Business Media LLC'
- Publication date
- Field of study
Design of efficacious somatic cell genome editing strategies for recessive and polygenic diseases
- Author
- A Herzog
- A Kulesa
- A Li
- AE Carpenter
- AL Firth
- AV Anzalone
- B Lee
- B Steyer
- B Wang
- BP Kleinstiver
- BP Kleinstiver
- C Albayrak
- C Seeger
- C Yu
- C-Q Song
- CD Richardson
- CD Sago
- CE Nelson
- CR Warren
- CT Charlesworth
- D Yang
- DBT Cox
- DG Ousterout
- DL Wagner
- E Liu
- E Martin-Touaux
- E van der Wal
- E van der Wal
- F Allen
- F Ran
- F Xu
- FA Ran
- H Azuma
- H Li
- H Yin
- H Yin
- H Zhu
- HW Yang
- IM Slaymaker
- IY Chen
- J Carlson-Stevermer
- J Carlson-Stevermer
- J Hemphill
- J Park
- J Sha
- J-A Lim
- J-A Ribeil
- JE Bond
- JG Doench
- JH Shin
- JW Youm
- K Saha
- KK Raval
- KM Davis
- L Villiger
- LB Harrington
- M Cui
- M Kosicki
- MK Cromer
- ML Maeder
- MP Zafra
- MW Popp
- MW Shen
- N Raben
- OA Bodamer
- P Kishnani
- PS Kishnani
- PS Kishnani
- R Cloney
- R Ibraheim
- RT Walton
- S Han
- S Hoops
- S Lin
- S Matsumoto
- S Matsumoto
- S Torriano
- SQ Tsai
- SSD Ravin
- T Gutschner
- T Harkness
- T Wei
- TT Duong
- V Pattanayak
- V Prakash
- VL Simhadri
- VT Chu
- WL Chew
- WT Hendriks
- X Lian
- X Liang
- Y Fukuhara
- Y Rui
- Y Yang
- YK Katare
- Publication venue
- 'Springer Science and Business Media LLC'
- Publication date
- Field of study
Extracellular vesicles: biology and emerging therapeutic opportunities
- Author
- A Bobrie
- A Bobrie
- A Clayton
- A Clayton
- A Mizrak
- A Montecalvo
- A Potolicchio
- A Savina
- BT Pan
- C Chavez-Muñoz
- C D'Souza-Schorey
- C Eken
- C Harding
- C Hsu
- C Liu
- C Raiborg
- C Théry
- CA Maguire
- CP-K Lai
- D Millimaggi
- D Sun
- DJ Gibbings
- DL Sprague
- DM Pegtel
- E Emmanouilidou
- ED Sverdlov
- EU Wieckowski
- F Chalmin
- F Collino
- G Camussi
- G Lachenal
- G Raposo
- H Sheldon
- H Valadi
- HF Dvorak
- HG Lamparski
- HHH Peinado
- I Del Conde
- I Monleón
- I Nazarenko
- Imre Mäger
- J Faure
- J Rak
- J Ratajczak
- J Skog
- J Wahlgren
- JC Gross
- JF Nabhan
- JM Aliotta
- JM Aliotta
- JW Kim
- K Al-Nedawi
- K Al-Nedawi
- K Trajkovic
- L Alvarez-Erviti
- L Biancone
- L Timmers
- L Timmers
- L Zitvogel
- LG Lima
- LJ Vella
- M Baj-Krzyworzeka
- M Baj-Krzyworzeka
- M Baj-Krzyworzeka
- M Chivet
- M Gnecchi
- M Gnecchi
- M Guescini
- M Hedlund
- M Kesimer
- M Logozzi
- M Mack
- M Mittelbrunn
- M Ostrowski
- M Szajnik
- M Yang
- Matthew J. A. Wood
- MB Herrera
- MC Deregibus
- MET Tesselaar
- MF Baietti
- MF Bolukbasi
- MZ Ratajczak
- N Chaput
- OG De Jong
- PJ Quesenberry
- Q Pan
- R Gastpar
- RC Lai
- RC Lai
- RWY Yeo
- S Bhatnagar
- S Bruno
- S Bruno
- S Bruno
- S El Andaloussi
- S Gatti
- S Ohno
- S Yu
- S-HH Kim
- SA Bellingham
- Samir EL Andaloussi
- SD Olson
- SN Chatterjee
- SS Sidhu
- TJ Beveridge
- TL Lentz
- TN Ellis
- TS Chen
- V Cantaluppi
- V Cantaluppi
- V Muralidharan-Chari
- VL Vega
- VR Simhadri
- W Zhu
- X Zhuang
- Xandra O. Breakefield
- Y Akao
- Y Lee
- Y Zhang
- Y-Y Jang
- Z Cai
- Publication venue
- 'Springer Science and Business Media LLC'
- Publication date
- Field of study
Immunogenicity of CAR T cells in cancer therapy
- Author
- A Di Stasi
- A Frazao
- A Heczey
- A Heczey
- A Hombach
- A Li
- A Muniappan
- A Schmidts
- AD Cohen
- AJ Kansagra
- AM Leen
- AR Haas
- B Hu
- B Potthoff
- B Savoldo
- BG Till
- BG Till
- C Arber
- C Berger
- C Imai
- CA Ramos
- CE Brown
- CH June
- CH Lamers
- CHJ Lamers
- CJ Turtle
- CJ Turtle
- CRJ Pameijer
- CT Charlesworth
- D Gomes-Silva
- D Moritz
- D Schneider
- DC Deniger
- DL Wagner
- DW Lee
- E Liu
- E Spierings
- E-M Jahn
- EA Stadtmauer
- EJ Suchin
- F Mo
- G Fucá
- G Shankar
- GG Gornalusse
- GG Klee
- GJ Jaffers
- GL Beatty
- H Mizuguchi
- H Torikai
- H Xu
- H Zhang
- I Blanco
- I Tzannou
- I Yakoub-Agha
- J Cao
- J Gauthier
- J Maher
- J Pan
- J Rasaiyaah
- J Ren
- J Scholler
- J Xu
- JH Cho
- JJ Lohmueller
- JJ Melenhorst
- JN Brudno
- JN Brudno
- JN Brudno
- JN Kochenderfer
- JS Miller
- K Sege
- KC Conlon
- KM Hege
- KM Mahadeo
- KS Kahlon
- KT Mueller
- L Mikkilineni
- LC Hill
- LM Whilding
- M Abou-El-Enein
- M Elsallab
- M Hegde
- M Hudecek
- M Jonnalagadda
- M Kalos
- M MacKay
- M Mamonkin
- M-Y Li
- MA Pule
- MC Jensen
- MH Kershaw
- MV Maus
- N Ahmed
- N Ahmed
- N Gonzales
- N Lam
- N Li
- N Raje
- NN Shah
- NN Shah
- NP Restifo
- P Holliger
- P Muranski
- PM Maciocia
- R Awasthi
- R Benjamin
- R Lanza
- RD Guest
- RG Majzner
- RP Junghans
- S Depil
- S DeWolf
- S Ghorashian
- S Rafiq
- S Sengupta
- SA Ali
- SA Grupp
- SC Clarke
- SL Maude
- SL Maude
- SL Maude
- SR Riddell
- SS Neelapu
- T Deuse
- T Gargett
- T Jain
- T Shum
- T Shum
- T Zhang
- T-S Kim
- TJ Fry
- V Baudouin
- V Wiebking
- VL Simhadri
- W Qasim
- W Wels
- W-H Zhao
- X Deng
- X Ma
- X Wang
- X Zhou
- X-H Zhang
- Y Chen
- Y Fu
- Y Kagoya
- Y Kagoya
- Y Lu
- Y Pacheco
- Y Yang
- Y Zhao
- Z Yan
- Publication venue
- 'Springer Science and Business Media LLC'
- Publication date
- Field of study