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1 research outputs found
INNOVATIVE SPLICE SWITCHING OLIGONUCLEOTIDE THERAPY FOR NIEMANN-PICK TYPE C1 DISEASE
Author
Daniel Ginberg
Haiyan Zhou
+7Â more
Mara Dierssen
Maria Martinez De Lagran
Marvin Caruthers
Ondrej Kostov
Paul Gissen
Timothy Yu
Yu-Han Huang
Publication venue
Elsevier
Publication date
01/10/2023
Field of study
No full text
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