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1 research outputs found
P005: Atidarsagene autotemcel (hematopoietic stem cell–gene therapy) preserves cognitive and motor development in metachromatic leukodystrophy with up to 12 years follow-up*
Author
Alan Richardson
Alberto Zambon
+24Â more
Alessandra Clerici
Alessandro Aiuti
Alessia Ippolito
Andrew Shenker
Elena Sophia Fratini
Eugenio Montini
Fabiola De Mattia
Francesca Ciotti
Francesca Fumagalli
Francesco Morena
Jean Brooks
Laura Campbell
Leslie Meltzer
Maddalena Fraschini
Marcella Facchini
Marina Sarzana
Muska Yarzi
Sabata Martino
Salvatore Recupero
Sara Locatelli
Sean Moro
Stefano Scarparo
Valeria Calbi
Vera Gallo
Publication venue
Elsevier
Publication date
01/01/2024
Field of study
No full text
Directory of Open Access Journals