3 research outputs found
Health-related quality of life in mucopolysaccharidosis: looking beyond biomedical issues
- Author
- A Riazi
- A Tanaka
- A Tylki-Szymanska
- AM Montaño
- AS Kunin-Batson
- BK Burton
- C Decker
- C Lampe
- C Lavery
- Centers for Disease Control and Prevention
- Christian J. Hendriksz
- Christina Lampe
- CJ Hendriksz
- CJ Hendriksz
- CJ Hendriksz
- CJ Hendriksz
- CJ Hendriksz
- DR Ramey
- E Braunlin
- E Davis
- E Jacob
- EG Shapiro
- EGH Verrips
- EM Bunge
- G Kobelt
- G Singh
- HY Lin
- I Kuratsubo
- J Marucha
- J Muenzer
- J Muenzer
- JB Holt
- JE Wraith
- Jeffrey I. Gold
- JW Varni
- JW Varni
- K White
- Kenneth I. Berger
- KJ Bjoraker
- KL Bergwerk
- LA Clarke
- LC Doward
- LM Breau
- M Beck
- M Beck
- M Kosinski
- M Needham
- M Needham
- M Orme
- M Raluy-Callado
- M Sifuentes
- M Solans
- MMG Brands
- MMMG Brands
- N Ali
- NR Guarany
- P Dolan
- P Harmatz
- P Harmatz
- P Harmatz
- P Harmatz
- P Harmatz
- Paul J. Orchard
- R Aslam
- R Giugliani
- Rebecca Southall
- S Tomatsu
- SA Jones
- SA Jones
- Sarah Long
- SJ Swiedler
- Stephen Sande
- Susanne G. Kircher
- T Kato
- The WHOQOL Group
- TM Palermo
- V Valayannopoulos
- Publication venue
- 'Springer Science and Business Media LLC'
- Publication date
- Field of study
Effects of Enzyme Replacement Therapy Started Late in a Murine Model of Mucopolysaccharidosis Type I
- Author
- A Arfi
- AD Dierenfeld
- AM Martins
- Angela Maria Vicente Tavares
- D Pan
- DA Wolf
- EA Braunlin
- EA Braunlin
- ED Kakkis
- EF Neufeld
- F Matthes
- FL Wilkinson
- G Baldo
- G Baldo
- G Baldo
- G Baldo
- G Baldo
- G Baldo
- Gabriela Pasqualim
- Guilherme Baldo
- H Harada
- J a Metcalf
- J Muenzer
- J Muenzer
- JA Lyons
- JE Jones
- JE Wraith
- JE Wraith
- JJ Boelens
- K D’Aco
- K Ohmi
- L Ou
- LA Clarke
- LD Archer
- M Beck
- M Sifuentes
- MH De Ru
- MH De Ru
- MH De Ru
- MMMG Brands
- MV Muñoz-Rojas
- O Gabrielli
- P Dickson
- R Giugliani
- R Giugliani
- R Giugliani
- Roberto Giugliani
- T Vieira
- Talita Giacomet de Carvalho
- Ursula Matte
- V Tokic
- V Valayannopoulos
- X Ma
- Publication venue
- 'Public Library of Science (PLoS)'
- Publication date
- Field of study
Patient and observer reported outcome measures to evaluate health-related quality of life in inherited metabolic diseases: a scoping review
- Author
- A Fabre
- A Graesdal
- A Martinuzzi
- A Martinuzzi
- A Mehta
- A Pisani
- A Sechi
- A Slade
- A. S. Kunin-Batson
- Agnes Rafalko
- AH Miners
- AM Bosch
- AM Bosch
- AT van der Ploeg
- B de Graaff
- B Hoffmann
- B Hoffmann
- B Hoffmann
- B Meiser
- BC Johnston
- BE Smid
- BJ Masek
- BW Bresnahan
- C Angelini
- C Cazzorla
- C Cazzorla
- C Lampe
- C Regnery
- C Verhaak
- Carlota Pascoal
- CB Langman
- CJ Hendriksz
- CM Eng
- CM Eng
- CM Mak
- CR Roe
- D Concolino
- D Elstein
- D Gungor
- D Gungor
- D Jamiolkowski
- D Munguia-Izquierdo
- D Oder
- D Orlikowski
- D Wild
- D.G. Kyte
- DA Hughes
- DA Hughes
- DA Laney
- DA Robbins
- Dietrich Matern
- Dorinda Marques-da-Silva
- DP Germain
- E Picavet
- E Rombout-Sestrienkova
- E Simon
- E Storch
- E Thimm
- E. C. Nelson
- EG Shapiro
- EMEA
- Ethan Basch
- EV Neto
- F Baehner
- F Ceravolo
- F Modersitzki
- FF Ulmer
- FL Oliveira
- G Cotugno
- GK Aslan
- GM Pastores
- H Arksey
- H Che
- H Eggink
- Healthy People 2020
- HR Mundy
- I Kantola
- I Wiklund
- J Cialone
- J Ghali
- J Muenzer
- J Picot
- J Vockley
- J-P Bonnefont
- Jaak Jaeken
- JCH van der Hilst
- JE Ware
- JL Ridgeway
- JW Koskenvuo
- K Splinter
- K Tsuboi
- K Tsuboi
- K Wyatt
- KF Gold
- KR Bogart
- L Hyttinen
- LA Clarke
- LB Wenzel
- LH Koens
- LM Millward
- LuĂsa Barros
- M Arends
- M Beck
- M Bevans
- M Bik-Multanowski
- M Brundage
- M Dinan
- M Gargiulo
- M Maia
- M MalĂ˝
- M PĂ©ntek
- M Raluy-Callado
- M Ries
- M Schaefer
- M Svetel
- M Wagner
- M Wastfelt
- MA Barba-Romero
- MA Landolt
- ME Huang
- MG Bouwman
- MJ Bennett
- MLC Hagemans
- MM Favejee
- MM McGovern
- MMG Brands
- MMMG Brands
- N Ali
- N Bonner
- N Bugescu
- N Guffon
- N Mata
- N Weinreb
- NA Mathiowetz
- NA Zeltner
- NA Zeltner
- NJ Street
- O Goker-Alpan
- P Giraldo
- P Giraldo
- P Giraldo
- P Giraldo
- P Gunther
- Paula A. Videira
- PR Harmatz
- PSS Kishnani
- R Feldmann
- Rita Francisco
- RJ Hopkin
- RN Komal Kumar
- RP Sutcliffe
- RY Wang
- S Assari
- S de Jongh
- S Demirdas
- S Strothotte
- S Verstovsek
- S Vielhaber
- S Wiebe
- Sandra Brasil
- SC Grunert
- SD Khangura
- T Guran
- T Merk
- T Watt
- TA Kanters
- TA Kanters
- TD Douglas
- TF Eminoglu
- TJ Weber
- Vanessa dos Reis Ferreira
- W Maselbas
- W Packman
- W Żuraw
- WR Wilcox
- Y Eto
- Y Okano
- Publication venue
- 'Springer Science and Business Media LLC'
- Publication date
- Field of study