3 research outputs found
RNA Therapeutics: How Far Have We Gone?
- Author
- A Aartsma-Rus
- A Akinc
- A Akinc
- A Berezhnoy
- A Dal Mas
- A Dal Mas
- A Digenio
- A Fire
- A Garanto
- A Goyenvalle
- A Goyenvalle
- A Hamilton
- A Heiser
- A Khvorova
- A MartĂnez-Pizarro
- A Matsui
- A Vulin
- A Wittrup
- A Wittrup
- AA D’Souza
- AD Ellington
- AD Judge
- AD Judge
- AE Emery
- AF McGettrick
- AG Fraser
- AJ Hamilton
- AJ Leger
- AL Brass
- AL Jackson
- AM Rossor
- AR Krol van der
- B Roehr
- B Shi
- B Weide
- B Wu
- B Zetsche
- BM Paterson
- BP Monia
- C Betts
- C Cogoni
- C Godfrey
- C Mattioli
- C Napoli
- C Querfeld
- C Tuerk
- CA Chiriboga
- CE Nelson
- Cervantes
- CF Bennett
- CF Xu
- D An
- D Balestra
- D Balestra
- D Bianchini
- D Gaudet
- D Gaudet
- D Gaudet
- D Ha
- D Hong
- D Peer
- D Peer
- D Scalet
- D Wu-Scharf
- DB Cornelio
- Demuere
- DM Kenski
- DS Krause
- DV Morrissey
- DV Morrissey
- DW Bartlett
- DY Hwang
- E Buratti
- E Buratti
- E Fernandez Alanis
- E Glaus
- E Lawitz
- E Mercuri
- E Schrom
- E Song
- E Song
- E Zorde Khvalevsky
- EC Hayden
- EC Solano
- EJ Ackermann
- F DeRosa
- F Rigo
- F Saad
- F Schmid
- F Schmid
- F Shabanpoor
- FJ Raal
- FJ Raal
- G Cecere
- G Hutvagner
- G McClorey
- G Monteleone
- G Tanner
- G Vitravene Study
- G Vitravene Study
- G Vitravene Study
- GJ Hannon
- Graham McClorey
- H Yin
- H Yin
- H Yin
- HL Janssen
- HR Buller
- Hulton et al.
- I Donadon
- I Grissa
- J Bruck
- J Bruun
- J Canton
- J Chery
- J Cruz-Toledo
- J Devoldere
- J Gilleron
- J Guiro
- J Kurreck
- J Lieberman
- J Luo
- J Moreno-Montanes
- J Rogers
- J Soutschek
- JA Bauman
- JA Rytlewski
- JB Cohen
- JC Salerno
- JE Zuckerman
- JH Chan
- JJ Rossi
- JK Nair
- JM Benitez-Del-Castillo
- JM Ervasti
- JM Silva
- JO McNamara 2nd
- JR Kennerdell
- JR Mendell
- JR Mendell
- JR Mendell
- K Fitzgerald
- K Fitzgerald
- Katyayani Tatiparti
- KJ Pasi
- KK Ray
- KL Sewell
- KM Schoch
- KN Chi
- KR Lim
- KĂĽbler et al.
- L Aagaard
- L Cong
- L Han
- L Hartmann
- L Lum
- L Matos
- L Meer van
- L Spraggon
- L Zangi
- LA Wheeler
- Libertine et al.
- M Baba
- M Baralle
- M Boutros
- M Gooding
- M Kortylewski
- M Manoharan
- M McCaleb
- M Millard
- M Nizzardo
- M Pinotti
- M Pinotti
- M Pinotti
- M Raponi
- M Robbins
- M Tabebordbar
- M Tajnik
- M.-F. Yuen
- MA Denti
- MA Denti
- MA Morse
- MA Morse
- Marc Suñé-Pou
- Maria Coutinho
- Marine Imbert
- ME Davis
- ME Rogalska
- ME Visser
- MG Stanton
- MH Ree van der
- MH Ree van der
- MJ Graham
- MJ Serramia
- MK Montgomery
- ML Bobbin
- MM Evers
- MM Haroon
- MP Czech
- MR Lerner
- MR Schlabach
- MS Falzarano
- MS Kormann
- N Pardi
- N Pfeiffer
- NC Lee
- NJ Caplen
- NJ Viney
- NM Goemans
- O Voinnet
- OB Suhr
- P Lönn
- P Mali
- P Miner
- P Odermatt
- P Sandy
- PB Duell
- PC Zamecnik
- PJ Paddison
- PP Toth
- PS Low
- QD Nguyen
- R Barrangou
- R Gabathuler
- R Gabathuler
- R Kole
- R Kole
- R Sorek
- R Sánchez-Alcudia
- RD Santos
- RF Ketting
- RJ Boado
- RL Juliano
- RS Finkel
- RS Finkel
- RS Geary
- S Bhanot
- S Buduru
- S Chowdhury
- S Cirak
- S Demirjian
- S Lefebvre
- S Patel
- S Ramaswamy
- S Tsimikas
- S Valadkhan
- S West
- S Wilgenhof
- SA Leachman
- Salzberg
- SC Semple
- SC Wong
- SD Jayasena
- SM Elbashir
- SM Elbashir
- SM Hammond
- SM Mount
- SM Rittig
- SMG Jirka
- ST Crooke
- Sterinu-Cercel
- T Coelho
- T Geib
- T Golan
- T Voit
- TB Kinane
- TC Roberts
- TI Cornu
- TM Miller
- Triozzi et al.
- TS Zimmermann
- Turner et al.
- U Sahin
- U Unniyampurath
- V Limmroth
- V Mittal
- V Peddi
- V Wally
- Valentina Sardone
- VV Oberemok
- W Tai
- WL Hwu
- WL Woerd van der
- X Gao
- X Roca
- X Roca
- X Roca
- Y Deng
- Y Granot
- Y Hua
- Y Hua
- Y Wang
- Y Yu
- Y Zhuang
- YL Chiu
- Zibiao Li
- Publication venue
- 'Springer Science and Business Media LLC'
- Publication date
- 25/07/2019
- Field of study
In recent years, the RNA molecule became one of the most promising targets for therapeutic intervention. Currently, a large number of RNA-based therapeutics are being investigated both at the basic research level and in late-stage clinical trials. Some of them are even already approved for treatment. RNA-based approaches can act at pre-mRNA level (by splicing modulation/correction using antisense oligonucleotides or U1snRNA vectors), at mRNA level (inhibiting gene expression by siRNAs and antisense oligonucleotides) or at DNA level (by editing mutated sequences through the use of CRISPR/Cas). Other RNA approaches include the delivery of in vitro transcribed (IVT) mRNA or the use of oligonucleotides aptamers. Here we review these approaches and their translation into clinics trying to give a brief overview also on the difficulties to its application as well as the research that is being done to overcome them.info:eu-repo/semantics/publishedVersio
A review of the process of knowledge transfer and use of evidence in reproductive and child health in Ghana
- Author
- A Sundaram
- AA Bawah
- AA Manu
- AA Manu
- AD Oxman
- AH Van de Ven
- AL Cochrane
- AR Oduro
- BR Kirkwood
- C Mitton
- C Tawiah-Agyemang
- CA Moyer
- CA Moyer
- CH Weiss
- CH Weiss
- CT Kapungu
- D Chandramohan
- D de Savigny
- D de Souza
- D Sinclair
- DM Campbell
- E Hall
- E Sevene
- EJ Power
- EK Nakua
- EKM Darteh
- EM Rogers
- ESK Morhe
- ET Dassah
- ET Dassah
- F Abdullah
- F Baiden
- F Sukums
- FS Achana
- G GYK
- G Tomson
- G Vance
- Ghana Health Service
- Ghana Health Service
- Ghana Health Service
- Ghana Health Service
- Ghana Health Service
- Ghana Health Service
- Ghana Health Service Ministry of Health
- Ghana Health Service UNFPA, UKaid
- Ghana Statistical Service (GSS) Ghana Health Service (GHS) and ICF International
- Gordon Abekah-Nkrumah
- ID Graham
- ID Graham
- J Bryce
- J Geynisman
- J Grimshaw
- J Hussein
- J Lavis
- J Lomas
- J Trostle
- JF Amoako
- JF Dowd
- JF Phillips
- JK Awoonor-Williams
- JK Awoonor-Williams
- JK Awoonor-Williams
- JN Lavis
- JN Lavis
- Johnson Ermel
- K Awusabo-Asare
- K Kikuchi
- K Oliver
- K Singh
- KK Adjei
- KM Edmond
- KM Edmond
- L Hulton
- L Reichenbach
- L Stinson
- L Subramanian
- LE Cofie
- Lokossou Virgil
- M Aaserud
- M Amoakoh-Coleman
- M Atuahene
- M Dobbins
- M Hennink
- M Kogan
- M Obrist
- M Whitehead
- MA Ako
- MA Albert
- MA Dalaba
- MI Amoakohene
- Ministry of Health
- Ministry of Health
- Ministry of Health
- Ministry of Health
- Ministry of Health
- Ministry of Health
- Ministry of Health
- Ministry of Health
- Ministry of Health
- Ministry of Health
- Ministry of Health (MOH) WHO GLOBALFUND
- Ministry of Health GHS, UNICEF, UNFPA, WHO, AMDD
- MJ Dobrow
- National Institute for Health and Clinical Excellence (NICE)
- NAY Twum-Danso
- NN Asundep
- NP Roos
- O Tulloch
- P Nyarko
- P Uvin
- PB Adongo
- PB Adongo
- RA Aborigo
- S Innvær
- S Witter
- SA Oppong
- SD Rominski
- SE Straus
- SH Masters
- SH Mayhew
- Sombié Issiaka
- SR Hanney
- T Okiwelu
- T Powell-Jackson
- TA Gaziano
- U Baker
- UNFPA
- V Lei
- V Shelus
- V Ward
- VN Orish
- W Friedman
- World Bank
- World Health Organization
- World Health Organization
- World Health Organization
- Z Hill
- Z Hill
- Ö Tunçalp
- Publication venue
- 'Springer Science and Business Media LLC'
- Publication date
- Field of study
Idiopathic Nephrotic Syndrome in Children: Clinical Aspects
- Author
- A Bagga
- A Bagga
- A Bagga
- A Bajpai
- A Doucet
- A El-Firjani
- A Fogo
- A Fornoni
- A Guasch
- A Gulati
- A Gulati
- A Gulati
- A Hammad
- A Magnasco
- A Martinez Vea
- A Meyrier
- A Mii
- A Moudgil
- A Pena
- A Prytula
- A Sakarcan
- A Schwarz
- A Singh
- A Sinha
- A Sinha
- A Tejani
- A Valanciute
- A Valeri
- A Zagury
- AA Ali
- AA Eddy
- AC Hsu
- AF Donia
- AF Michael
- AH Cohen
- AH Nagi
- AJ Donker
- AJ Howie
- AJ McAdams
- AJ Voets
- AL Sellier-Leclerc
- AL Sellier-Leclerc
- AL Sellier-Leclerc
- AL Sellier-Leclerc
- AM Krensky
- AO Muda
- AR Watson
- AS Abeyagunawardena
- AS Abeyagunawardena
- AS Abeyagunawardena
- AT Lahdenkari
- B Cammas
- B Meijers
- B Montane
- B Taylor
- BA Kerlin
- BA Kerlin
- BA Kerlin
- BJ Carrie
- BM Tune
- BM Tune
- British Association for Paediatric Nephrology
- C Faul
- C Kleinknecht
- C Nakahara
- C Norero
- C Polito
- C Ponticelli
- C Ponticelli
- C Ponticelli
- C Wei
- CF Sier
- CM Toth
- D Cathelin
- D Fliser
- D Haffner
- D Hristea
- D Sahali
- D Sahali
- DB Thomas
- DC Wheeler
- DK Rajpoot
- DM Clive
- DS Ardelean
- DS Gipson
- DS Gipson
- DS Milliner
- E Erkan
- E Grishman
- E Ingulli
- E Ingulli
- E Ingulli
- E Ingulli
- E Ritz
- E Smet De
- EB Trainin
- EH Garin
- EH Garin
- EH Garin
- EH Jenis
- EI Feinstein
- EJ Nehus
- EL Ramos
- EM Dorresteijn
- EM Hodson
- EM Hodson
- EM Hodson
- EM Kim
- EM Ruth
- EP Leumann
- ER Schlesinger
- ET McCarthy
- F Cavagnaro
- F Emma
- F Fakhouri
- F Fencl
- F Vincenti
- FB Waldo
- G Banfi
- G Barbano
- G Canaud
- G Cara-Fuentes
- G Lagrue
- G Lagrue
- G Rizzoni
- GM Barletta
- GS Arbus
- GS Markowitz
- H Alpay
- H Ito
- H Kawaguchi
- H Mansour
- HA Kyrieleis
- HJ Baluarte
- HK Yap
- HM Coovadia
- HR Powell
- I Anochie
- I Novak
- J Bariety
- J Born van den
- J Chiu
- J Churg
- J Dantal
- J Gellermann
- J Giangiacomo
- J Joven
- J Ksiazek
- J Laufer
- J Laurent
- J McDonald
- J Mowry
- J Penso
- J Pinto
- J Reiser
- J Rodriguez-Soriano
- J Vande Walle
- J Zachwieja
- JA Jefferson
- JA Kari
- JA Velosa
- JB Palcoux
- JC Davin
- JC Jennette
- JE Striegel
- JG Berg Van Den
- JG Mongeau
- JH Ehrich
- JH Ehrich
- JK Deegens
- JK Deegens
- JM Morales
- JM Yabu
- JP Hayslett
- JR Hoyer
- JS Cameron
- JS Cameron
- JW Chang
- JW Eagen
- JY Doe
- K Afzal
- K Al-Saran
- K Dittrich
- K Iijima
- K Iijima
- K Ishikura
- K Ishikura
- K Kamei
- K Kawano
- K Latta
- K Loeffler
- K Murnaghan
- K Nozu
- K Scharer
- K Sgambat
- KA Sato
- KH Paik
- KN Lai
- KP Mehta
- KV Lieberman
- L Barisoni
- L Barisoni
- L Berre Le
- L Delbe-Bertin
- L Raij
- LF Ferder
- LJ Zhang
- LR Hyman
- M Artero
- M Bak
- M Broyer
- M Elisaf
- M Freundlich
- M Freundlich
- M Kashgarian
- M McVicar
- M Morita
- M Pradhan
- M Razzak
- M Sato
- MA Lewis
- MA Nash
- MA Saleem
- MA Thabet
- MB Leonard
- MB Stokes
- MC Chaumais
- MD Pescovitz
- MD Sinha
- ME Bock
- ME Salsano
- MG Seikaly
- MI Lilova
- MJ Gregory
- MJ Kemper
- MJ Kemper
- MJ Kemper
- MJ Schoeneman
- N Prasad
- N Schlegel
- N Sidenius
- N Teeninga
- N Teeninga
- N Ueda
- N Ueda
- ND Vaziri
- ND Vaziri
- NE MacDonald
- NJ Siegel
- NK Biyikli
- O Boyer
- O Boyer
- O Koskimies
- P Cochat
- P Grimbert
- P Grimbert
- P Hari
- P Niaudet
- P Niaudet
- P Niaudet
- P Niaudet
- P Ravani
- P Ruggenenti
- P Senggutuvan
- P Tanphaichitr
- P Tarshish
- PA McKinney
- PD Thomson
- PD Yorgin
- PF Hoyer
- PF Hoyer
- PK Cheung
- PT McEnery
- R Bhimma
- R Dall’Amico
- R Drachman
- R Elhence
- R Habib
- R Habib
- R Habib
- R Habib
- R Lennon
- R Salomon
- R Waldherr
- RH Raafat
- RH White
- RJ Hogg
- RJ Maas
- RJ Shalhoub
- RK Alwadhi
- RK Detwiler
- RM Haws
- RM Lombel
- RN Fine
- RN Srivastava
- RN Srivastava
- RP Woroniecki
- RR Verani
- RS Trompeter
- RS Trompeter
- S Azib
- S Choudhry
- S Dundon
- S Fujinaga
- S Fujinaga
- S Gulati
- S Gulati
- S Ito
- S Ito
- S Leisti
- S Mendizabal
- S Sever
- S Tanawattanacharoen
- S Westphal
- SA Hulton
- SA Mendoza
- SA Williams
- SD Kim
- SE Maizel
- SJ Shankland
- SL Furth
- SM Cueto
- SO Bohman
- SR Meadow
- SR Wynn
- SW Zimmerman
- SY Zhang
- T Apeland
- T Hirano
- T Kersnik Levart
- T Ulinski
- T Wada
- TK Mattoo
- TL Donatti
- TN Meyer
- U Dayal
- U Vester
- V Audard
- V Audard
- V Baudouin
- V Guigonis
- VD D’Agati
- VJ Savin
- VJ Savin
- VR Mello de
- W Huppes
- W Rascher
- W Wang
- W Wong
- WA Prescott Jr
- WE Grupe
- WG Couser
- WM Bennett
- WP Rennert
- WW Bakker
- WW Bakker
- WY Ding
- Y Kitano
- Y Pirson
- Publication venue
- 'Springer Science and Business Media LLC'
- Publication date
- Field of study