CORE
🇺🇦Â
 make metadata, not war
Services
Services overview
Explore all CORE services
Access to raw data
API
Dataset
FastSync
Content discovery
Recommender
Discovery
OAI identifiers
OAI Resolver
Managing content
Dashboard
Bespoke contracts
Consultancy services
Support us
Support us
Membership
Sponsorship
Community governance
Advisory Board
Board of supporters
Research network
About
About us
Our mission
Team
Blog
FAQs
Contact us
Filters
1 research outputs found
Hematopoietic stem cell gene therapy leads to marked visceral organ improvements and a delayed onset of neurological abnormalities in the acid sphingomyelinase deficient mouse model of Niemann–Pick disease
Author
A Rousseau
A Vellodi
+42Â more
B Otterbach
B Scaggiante
C Fillat
CM Simonaro
D Markowitz
D Markowitz
D Newrzella
DB Arnold
DC German
DM Bodine
E Bayeuer
EH Schuchman
EH Schuchman
EH Schuchman
I Bertoncello
JC Gartner
K Horinouchi
K Horinouchi
L Singh
M Dao
M Goerner
MK Chuah
MM Huang
MR Koller
N Eliopoulos
P Daloze
PB Schneider
PL Yeyati
PM Hoogerbrugge
RO Brady
S Furuya
S Nakagawa
S Okada
S Stein
SL Schissel
SRP Miranda
SRP Miranda
SRP Miranda
T Dinur
TA Kuemmel
W Brugger
W Krivit
Publication venue
'Springer Science and Business Media LLC'
Publication date
Field of study
No full text
Crossref