6 research outputs found
Established cell surface markers efficiently isolate highly overlapping populations of skeletal muscle satellite cells by fluorescence-activated cell sorting
- Author
- A Asakura
- A Gromova
- A Mauro
- A Sacco
- AS Brack
- AW Joe
- C Lepper
- D Bosnakovski
- D Hardy
- DD Cornelison
- DDW Cornelison
- DH Stitelman
- H Yin
- JL Shadrach
- JR Beauchamp
- L Liu
- M Cerletti
- M Cerletti
- MJ Conboy
- MR Chapman
- N Ieronimakis
- N Motohashi
- NA Dumont
- P Rocheteau
- P Seale
- R Abou-Khalil
- RI Sherwood
- S Biressi
- S Biressi
- S Chargé
- S Fukada
- SP Perfecto
- T Yoshida
- TH Cheung
- Publication venue
- 'Springer Science and Business Media LLC'
- Publication date
- Field of study
Animal Models for Prenatal Gene Therapy: Rodent Models for Prenatal Gene Therapy
- Author
- Publication venue
- 'Springer Science and Business Media LLC'
- Publication date
- Field of study
Improved precision in the analysis of randomized trials with survival outcomes, without assuming proportional hazards
- Author
- A Rotnitzky
- AA Tsiatis
- AW van der Vaart
- B Efron
- Daniel F. Hanley
- DB Rubin
- DF Hanley
- DH Wolpert
- DR Cox
- EJ Williamson
- Elizabeth Colantuoni
- H Bang
- Iván DĂaz
- J Hahn
- J Pfanzagl
- J Xie
- JC Brooks
- JM Robins
- JM Robins
- KL Moore
- KL Moore
- L Parast
- L Tian
- L Zhao
- M Schemper
- M van der Laan
- M Zhang
- M Zhang
- Michael Rosenblum
- MJ van der Laan
- MJ van der Laan
- MJ van der Laan
- OM Stitelman
- P Royston
- P-Y Chen
- PJ Bickel
- S Gruber
- SR Cole
- SR Cole
- W Cao
- X Bai
- X Lu
- Z Tan
- Z Tan
- Publication venue
- 'Springer Science and Business Media LLC'
- Publication date
- Field of study
Early intra-amniotic gene transfer using lentiviral vector improves skin blistering phenotype in a murine model of Herlitz junctional epidermolysis bullosa
- Author
- A Nakano
- A Radu
- A W Flake
- A Weissman
- AM Douar
- C Byrne
- C Matsui
- C Matsui
- C Muhle
- C Muhle
- CK Kaufman
- D Hata
- DH Stitelman
- DT Woodley
- E Fuchs
- ED Zanjani
- ES Reynolds
- F Mavilio
- G Cotsarelis
- H Schneider
- J McGrath
- J Qiujie
- J Remington
- J Tolar
- J Uitto
- J Uitto
- J Uitto
- J Yoshizawa
- JE Kuster
- JE Wagner
- JR Stanley
- K Tamai
- M Aumailley
- M Endo
- M Endo
- M Endo
- M Endo
- M Endoh
- M Ito
- M Laimer
- M Laimer
- M Sato
- MG Kim
- N Sakai
- P M Marinkovich
- P W Zoltick
- RE Billingham
- RM Lavker
- S Amano
- SN Waddington
- T Chino
- T Henriques-Coelho
- T Wong
- V Levy
- XF Qin
- Publication venue
- 'Springer Science and Business Media LLC'
- Publication date
- Field of study
In Utero Gene Therapy and Genome Editing
- Author
- A David
- A Majowicz
- C Zincarelli
- CD Porada
- CE Nelson
- CN Mattar
- CNZ Mattar
- D Wang
- DE Sabatino
- DH Stitelman
- DJ Carr
- DJ Carr
- DJ Garrett
- DL Ouellet
- DP Reay
- E Colletti
- F Mingozzi
- H Ma
- H Potter
- H Sugano
- H Yin
- H Yin
- J Bennett
- J Wang
- JA Zuris
- JL Roybal
- JS Shen
- KN Abi-Nader
- L Cong
- L Joyeux
- L Lisowski
- L Meertens
- L Naldini
- LA George
- LE Rosen
- M Endo
- M Endo
- M Jinek
- M Jinek
- M Sheppard
- M Simonsen
- M Tabebordbar
- MG Davey
- ML Maeder
- MR Dilworth
- MR Lieber
- N Ah Mew
- ND Tran
- NS Dejneka
- P Mali
- PE Hodges
- PJ Park
- R Calcedo
- R Calcedo
- R Sorek
- R Witt
- RD Owen
- RE Billingham
- S Arnould
- S Grizot
- S Lin
- SG Keswani
- SN Waddington
- T Krishnan
- WD Heyer
- X Han
- XD Han
- Y Wu
- Y Yang
- YS Ahi
- Publication venue
- 'Springer Science and Business Media LLC'
- Publication date
- Field of study
Genome engineering: a new approach to gene therapy for neuromuscular disorders
- Author
- A Aartsma-Rus
- A Abu-Baker
- A Akopian
- A Asokan
- A Asokan
- A Goyenvalle
- A Goyenvalle
- A Izmiryan
- A Lek
- A Lombardo
- A Oldfors
- A Onori
- A Onori
- AC Mercer
- AF Klein
- AJ Bogdanove
- AL Arnett
- AM Davie
- AM Kabadi
- AR Amenta
- B Brais
- B Brais
- B Palmieri
- B Ravikumar
- B Shen
- B Udd
- B Udd
- B Udd
- B Wang
- BF Benabdallah
- BL Stoddard
- BM Godinho
- BP Kleinstiver
- C Gerard
- C Long
- C Long
- C Sollu
- C Wijmenga
- C Zhao
- CA Gersbach
- CA Ross
- CD Carvin
- CE Nelson
- CE Nelson
- CG Bonnemann
- CH Vannoy
- Charles A. Gersbach
- Christopher E. Nelson
- CI Wooddell
- CL Himeda
- CS Young
- D DiMatteo
- D Gabellini
- D Gabellini
- D Hockemeyer
- D Madsen
- D Mittelman
- D Wang
- DA Persons
- DB Cox
- DE Bowles
- DG Ousterout
- DG Ousterout
- DG Ousterout
- DH Stitelman
- DJ Glover
- DM McCarty
- DR Deyle
- DU Kemaladewi
- E Deltcheva
- E Kimura
- F Mingozzi
- F Mingozzi
- F Mingozzi
- F Schmidt
- F Zhang
- FA Ran
- FD Urnov
- FS Tedesco
- G De Michele
- G Silva
- G Strimpakos
- G Xia
- G Zhang
- GF Richard
- GF Richard
- GF Richard
- H Foster
- H Koike-Yusa
- H Li
- H Wang
- H Yin
- H Yin
- HG Harley
- HH Yu
- HJ Lee
- HL Li
- I Faravelli
- I Maggio
- I Maggio
- IB Hilton
- IE Verhaart
- IM Slaymaker
- J Ashworth
- J Boch
- J Hartmann
- J Larkindale
- J Liu
- J Liu
- J Tinsley
- JA Doudna
- JA Zuris
- Jacqueline N. Robinson-Hamm
- JB Doyon
- JC Miller
- JC van Deutekom
- JC van Deutekom
- JD Brook
- JE Davies
- JM Tinsley
- JN Robinson-Hamm
- JP Iyombe-Engembe
- JR Mendell
- JR Mendell
- JT Seto
- JT Seto
- K Bushby
- K Gruber
- K Inagaki
- K Suzuki
- KD Foust
- KD Foust
- KE Davies
- KF Buckland
- KR Thomas
- KS Makarova
- L Colleaux
- L Cong
- L Popplewell
- L Riolobos
- L Xu
- L Xu
- L Yang
- LA Gilbert
- LE Rosen
- LM Wallace
- LM Wallace
- M Christian
- M Garriga-Canut
- M Hermann
- M Holkers
- M Jinek
- M Krahn
- M Liu
- M Mahadevan
- M Tabebordbar
- M Victor
- M Yu
- MA Kotterman
- MA Passini
- MG Di Certo
- MH Porteus
- MJ Moscou
- MJ Wood
- ML Maeder
- ML Maeder
- ML Maeder
- N Corbi
- N Maheshri
- NA McNeer
- NE Bengtsson
- NM Goemans
- NP Pavletich
- O Shalem
- O Smithies
- P Chapdelaine
- P Chapdelaine
- P Genovese
- P Harish
- P Kasparek
- P Perez-Pinera
- P Perez-Pinera
- P Romer
- P Rouet
- P Shelbourne
- P Tebas
- PC Sondergaard
- PD Hsu
- PG van Overveld
- PI Thakore
- PI Thakore
- PN Porensky
- Q Liu
- QL Lu
- QL Lu
- R Barrangou
- R Barrangou
- R Darabi
- R Moore
- R Morbitzer
- R Schroder
- R Tawil
- R Tupler
- RC DeKelver
- RD Cohn
- RJ Lemmers
- RM Gordley
- RM Quadros
- RR Beerli
- RR Beerli
- RS Finkel
- S Al-Zaidy
- S Arnould
- S Bortolanza
- S Cirak
- S Corti
- S Duque
- S Kay
- S Perie
- S Remy
- S Shen
- S Turan
- SA Wolfe
- SB Geutskens
- SE Raper
- SJ Brouns
- SJ Feeney
- SM Faust
- SN Pandey
- SQ Tsai
- T Cermak
- T Sato
- T Wang
- TA Rando
- TL Wu
- V Campuzano
- VR Arruda
- W Li
- W Lostal
- W Zhang
- WL Chew
- Y Cai
- Y Chen
- Y Zhang
- Y Zhou
- YG Kim
- YJ Li
- Z Wang
- Z Wu
- Z Wu
- Publication venue
- 'Springer Science and Business Media LLC'
- Publication date
- Field of study