Pressure for drug development in lysosomal storage disorders – a quantitative analysis thirty years beyond the US orphan drug act

By Konstantin Mechler, William K Mountford, Georg F Hoffmann and Markus Ries

Publisher: Springer Nature

Year: 2015

DOI identifier: 10.1186/s13023-015-0262-5

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Provided by: MUCC (Crossref)

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